The Most Expensive Drug  in the US is a Rare-Disease Game Changer

Hello! It’s Angelica in Boston. A new multimillion-dollar gene therapy promises to transform the lives of those with a rare blood disorder. But first...

US regulators recently approved a gene therapy that could vastly improve the lives of people with a rare blood disorder called beta thalassemia. At $2.8 million per treatment, the drug, called Zynteglo, vaults to the top of the list of most-expensive drugs ever to be sold in the US.