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The Most Expensive Drug in the US is a Rare-Disease Game Changer

Bluebird Bio Chief Executive Andrew Obenshain

Bluebird Bio Chief Executive Andrew Obenshain

Source: Bluebird Bio

Hello! It’s Angelica in Boston. A new multimillion-dollar gene therapy promises to transform the lives of those with a rare blood disorder. But first...

US regulators recently approved a gene therapy that could vastly improve the lives of people with a rare blood disorder called beta thalassemia.  At $2.8 million per treatment, the drug, called Zynteglo, vaults to the top of the list of most-expensive drugs ever to be sold in the US.